Gene therapy is linked to better nonmotor outcomes in spinal muscular atrophy type 1 compared to first-line nusinersen, new ...

Spinal muscular atrophy affects all the body's muscles. For a long time, it was considered a disease caused solely by the ...

Spinal muscular atrophy affects all the body’s muscles. For a long time, it was considered a disease caused solely by the ...

Kaitlin Batley, MD, a pediatric neurologist at Children’s Health and assistant professor at UT Southwestern Medical Center, discusses the importance of multidisciplinary care in spinal muscular ...

The Delhi High Court on Thursday upheld a single judge's refusal of an interim injunction sought by Swiss pharmaceutical ...

In what is being termed a major victory, Natco Pharma has won a legal battle against Swiss pharma giant Roche, allowing the ...

As their 8-month-old daughter prepares for gene therapy treatment, a Coon Rapids family is bracing for three months of ...

Spinal muscular atrophy is a rare genetic disease of the nerve cells in the spinal cord that can appear as early as infancy. The disease leads to a progressive loss of muscle strength. Those affected ...

Swiss pharmaceutical giant F Hoffmann-La Roche AG has approached the Supreme Court against the Delhi High Court's order allowing Natco Pharma to manufacture and sell a generic drug of Risdiplam, ...

The Delhi High Court has dismissed Roche's appeal, allowing Natco to launch a generic version of Risdiplam for spinal ...

A new clinical trial has revealed encouraging results for a muscle-targeting therapy aimed at improving motor function in children and adolescents with spinal muscular atrophy, according to a study ...