Spinal muscular atrophy affects all the body’s muscles. For a long time, it was considered a disease caused solely by the loss of nerve cells in the spinal cord. Now, a research team at Leipzig ...
FOX 9 Minneapolis-St. Paul on MSN
Coon Rapids family fights rare genetic disease to save daughter's life
As their 8-month-old daughter prepares for gene therapy treatment, a Coon Rapids family is bracing for three months of ...
Ahmedabad: Zydus Lifesciences Limited has received final approval from the United States Food and Drug Administration (USFDA) ...
AZoLifeSciences on MSN
Advances in Gene Silencing and Editing for Rare Disorders
Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...
Data from first cohort of five participants suggest an acceptable safety profile for AB-1003 in participants with limb-girdle muscular dystrophy (LGMD) 2I/R9, with no dose-limiting toxicities or ...
Today, Sammy is 17 years old and working hard to be able to walk across the stage at her high school graduation next spring. Whether kids like Sammy can achieve their dreams depends on whether ...
Early research suggests a brain test may predict whether antidepressants will cause sexual dysfunction. There has never been ...
News Medical on MSN
Study uncovers cerebellar involvement and social impairment
Spinal muscular atrophy is a rare genetic disease of the nerve cells in the spinal cord that can appear as early as infancy. The disease leads to a progressive loss of muscle strength. Those affected ...
Research Triangle Park, North Carolina Saturday, October 4, 2025, 13:00 Hrs [IST] ...
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