The director of UVA’s treatment program sees reason for “cautious optimism” after a small study’s positive results.
Eric Dane advocated for a cure for Amyotrophic Lateral Sclerosis (ALS) as the progression of his symptoms was on full display in a campaign video. After the “Euphoria” actor missed the planned “Grey’s ...
Gene therapies for rare diseases are frequently developed then discarded by drug companies because they can’t afford to produce the treatment for more patients. Gene therapies for rare diseases are ...
Our weekly roundup of the latest science in the news, as well as a few fascinating articles to keep you entertained over the ...
Cure Rare Disease Secures FDA Orphan Drug Designation for Investigational Gene Therapy to Treat Limb-Girdle Muscular Dystrophy Type R9 (LGMD2i/R9) Designation supports development of CRD-003, an ...
WOODBRIDGE, Conn.--(BUSINESS WIRE)--Cure Rare Disease (CRD), a 501(c)(3) nonprofit biotechnology company developing genetic therapies for ultra-rare neuromuscular diseases, today announced that the ...
Actor Eric Dane called for more funding for ALS research in a new video released on Monday, just months after he revealed he was diagnosed with the condition, commonly known as Lou Gehrig's disease.
A benefit concert is being held for San Angelo siblings who are battling a devastating illness together. Cory and Kelsea Turnbull are both living with Huntington’s disease, a rare and fatal genetic ...
On this episode of The David Frum Show, The Atlantic’s David Frum opens with reflections on President Donald Trump’s repeated delays to enforce the congressionally mandated TikTok ban. He explains how ...
In 2021, 57 million people across the planet were living with dementia. This class of memory-related diseases is the world’s seventh greatest killer, and Alzheimer’s disease is its most common form.
A groundbreaking discovery reveals how HIV integrates its genetic material into human DNA, exposing a key viral vulnerability that could lead to new therapies and bring the world closer to a ...