For decades, gene-editing science has been limited to making small, precise edits to human DNA, akin to correcting typos in ...

These chains come in a wide range of lengths. In humans a typical protein is about 400 amino acids long; some are a lot longer. Molecules of RNA, one of the two nucleic acids, can reach up to 100,000 ...

Inherited metabolic diseases are rare monogenic conditions that disrupt biochemical pathways, affecting energy production and ...